Official NIH NLM MEDLINE / PubMed Citation • PMID: 42913682
Efficacy and safety of mitapivat in patients with sickle cell disease (RISE UP): a phase 3, double-blind, global, randomised, placebo-controlled trial.
Lancet
Verbatim Formal Study Abstract
A total of 207 patients were randomly assigned to mitapivat (138 [67%]) or placebo (69 [33%]).